Gene editing has delivered remarkable results against sickle cell disease. Now researchers are working to make these personalized treatments faster, cheaper, and available to far more patients.

Gene therapy has changed what is possible for people living with sickle cell disease. New treatments have shown that the ...

Right now, approximately 20 billion red blood cells are busy traveling through your blood vessels. They are delivering oxygen to all the different tissues in your body and removing carbon dioxide to ...

Gene therapy is offering new hope for people with sickle cell disease. Here's how Virginia's latest Medicaid funding could ...

A Nashville doctor helped pioneer an FDA approved "state-of-the-art" gene-editing therapy that could be a cure for painful ...

In a Wednesday news release, the FDA announced it had approved Casgevy, the first gene therapy for children with sickle cell ...

Learn how gene editing is transforming sickle cell disease treatment and why expanding access to younger children matters.

Sickle cell disease refers to a group of genetic diseases that impact a protein that ferries oxygen through the blood. That protein is called hemoglobin, and in sickle cell disease, aberrant ...

Scientists from Johns Hopkins Medicine and eight other institutions in the United States, Africa and Europe say they have identified a potential new gene target that could be edited to treat sickle ...

The curing sickle cell through gene therapy story is a long way from being written. But it’s for sure that it has not gone ...

When Dr. Ambroise Wonkam walked into a panel on medical genetics out of curiosity, he had no idea it would shape the course of his career. Born in Cameroon, Wonkam has dedicated his career to studying ...

The study failure costs Agios a chance to one-up Novo Nordisk and represents yet another setback in a disease that’s ...