Six patients with glycogen storage disease type Ia have received a single infusion of BEAM-301, an in vivo base editor ...

Researchers built a three-layer human blood-vessel model that shows how fibroblasts amplify the vascular pathology of ...

Researchers have used CRISPR-Cas9 to remove CD28 from donor T cells and prevent fratricide before equipping them with ...

Wave Life Sciences has reached alignment with the US Food and Drug Administration on a registrational pathway for WVE-006, a GalNAc-conjugated RNA editing oligonucleotide for alpha-1 antitrypsin ...

Researchers built a three-layer human blood-vessel model that shows how fibroblasts amplify the vascular pathology of Hutchinson-Gilford progeria... Clinical: FDA Backs Single-Trial Pathway for ...

Researchers in Germany have identified a SOX9-responsive regulatory route to IRF6, a major orofacial-cleft risk gene, in cranial neural crest cells rather than only in oral epithelium. CRISPR-Cas9 ...

The minimal residual disease-positive cohort opens as part of the pivotal-stage development of Soficabtagene Geleucel (Sofi-cel), an off-the-shelf CAR-T cell therapy under evaluation for relapsed or ...

A mutation-agnostic CRISPR-Cas strategy that inserts a functional rhodopsin coding sequence into the human RHO locus has preserved retinal structure, function and visual acuity for a full year in a ...

A UCL-led team has developed a clinical-scale CRISPR-Cas9-AAV6 workflow intended to correct Wiskott-Aldrich syndrome in haematopoietic stem and progenitor cells, reaching 61% knock-in in more than 100 ...

Merck & Co. will present new single-cell functional genomics data generated using purpose-built assays developed with Mission Bio’s Assay Services team. Incyte will share updated clinical single-cell ...

Dixon joins as an independent Board member, adding deep healthcare finance and transaction expertise as VedaBio enters its next phase of growth SAN DIEGO--(BUSINESS WIRE)--VedaBio, a pioneering ...

CRISPR AgroBio News (CARBON) - an emerging initiative from CRISPR Medicine News - brings you the latest news on how CRISPR can shape agriculture for the future to guarantee food security in times of ...