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Duchenne Muscular Dystrophy
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O pequeno Lorenzo Silveira, de 10 anos, foi diagnosticado há três anos com distrofia muscular de #Duchenne (DMD). A doença paralisa progressivamente o funcionamento dos músculos do corpo, afetando até o coração e os pulmões. O progresso da doença, porém, pode ser detido com o uso de um remédio que foi aprovado este mês no Brasil pela Anvisa. O problema, porém, é o custo do tratamento: só o #medicamento custa 3,2 milhões de dólares, aproximadamente R$ 19 milhões na cotação atual. Duchenne é uma d
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